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Saffari, Afshin ; Brösse, Ines ; Wiemer-Kruel, Adelheid ; Wilken, Bernd ; Kreuzaler, Paula ; Hahn, Andreas ; Bernhard, Matthias K. ; van Tilburg, Cornelis M. ; Hoffmann, Georg F. ; Gorenflo, Matthias ; Hethey, Sven ; Kaiser, Olaf ; Kölker, Stefan ; Wagner, Robert ; Witt, Olaf ; Merkenschlager, Andreas ; Möckel, Andreas ; Roser, Timo ; Schlump, Jan-Ulrich ; Serfling, Antje ; Spiegler, Juliane ; Milde, Till ; Ziegler, Andreas ; Syrbe, Steffen (2019) Safety and efficacy of mTOR inhibitor treatment in patients with tuberous sclerosis complex under 2 years of age – a multicenter retrospective study. Orphanet journal of rare diseases, 14 (96). pp. 1-13. ISSN 1750-1172